Larimar doses adolescents in nomlabofusp paediatric pharmacokinetic run-in study for patients with Friedreich’s ataxia: Bala Cynwyd, Pennsylvania Saturday, January 25, 2025, 15: ...
Adolescents receive a weight-based dose equivalent to the 50 mg adult dose ; Adolescents 12-17 years old who complete participation in the pharmacokinetic (PK) run-in study will b ...
Larimar’s lead compound, nomlabofusp, is being developed as a potential treatment for Friedreich's ataxia. Larimar also plans to use its intracellular delivery platform to design other fusion ...